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Navigating Gene Therapy Commercialization in Europe: A Q&A with Novartis’ Joshi Venugopal

Navigating Gene Therapy Commercialization in Europe: A Q&A with Novartis’ Joshi Venugopal

Navigating Gene Therapy Commercialization in Europe A Q&A with Joshi Venugopal, General Manager of Gene Therapies and Rare Diseases, Europe Opinions expressed here are personal and not that of Novartis* Gene therapies…

RARE DISEASE CLINICAL TRIALS: A Collaborative Approach to Design and Execution

RARE DISEASE CLINICAL TRIALS: A Collaborative Approach to Design and Execution

Rare Disease Clinical Trials A Collaborative Approach to Design and Execution Patients who suffer from rare diseases need access to effective and safe medications. Given the low incidence of the diseases, the…

Demystifying the Maze: Centralized vs. National Procedures for Rare Disease Drug Registration in the EU

Demystifying the Maze: Centralized vs. National Procedures for Rare Disease Drug Registration in the EU

Demystifying The Maze Centralized vs. National Procedures for Rare Disease Drug Registration in the EU Introduction The European market presents a compelling opportunity for US pharma and biotech companies developing life-changing therapies…

Expanding into Europe

Expanding into Europe

Cracking the EMA Code Expanding into Europe Expanding a Rare Disease drug’s marketing authorization into Europe can potentially increase a company’s net worth, but it’s not a guaranteed outcome. Here’s a breakdown…

The Ultimate Guide to EMA Approval for Rare Disease Therapies: Unlocking European Access

The Ultimate Guide to EMA Approval for Rare Disease Therapies: Unlocking European Access

Your Ultimate Parter for EMA Approval of Rare Disease Therapies Unlocking European Access Developing a therapy for a rare disease is a noble endeavour, but the path to market is complex, especially…

The Geopolitics of Hope

The Geopolitics of Hope

The Geopolitics of Hope A Flourishing Market, Yet Millions in Europe Lack Access to Rare Disease Treatments Did you know that over 30 million people in Europe live with a rare disease,…